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Monogenic and Polygenic

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GENE replacement

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  • Monogenic and Polygenic

    Depending on the disease or disorder, it
    can be inherited from one or both parents.
    Or, sometimes it’s a change that just
    happens randomly. Audio: Español Subtitle: English

  • AAV vectors

    Time is critical because once cells lose
    their ability to function properly, they
    may not be able to be fixed, and any
    damage already done to the body may be
    irreversible. Audio: Spanish; Subtitle: English
    El tiempo es crítico porque una vez que las células pierden
    su capacidad de funcionar c...

  • AAV vectors targets

    AAVs are able to travel through the body
    to target many different kinds of cells.